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CHOP Researchers Develop Innovative Model Offering New Insights to Improve and Overcome Current Obstacles in Hemophilia A Gene Therapy
Researchers at CHOP announced the results of a new study offering insights into the development of next-generation gene therapies to treat hemophilia A.
Children’s Hospital of Philadelphia and Sidra Medicine to Establish First-Ever Pediatric Bone Marrow Transplant Program in Qatar
CHOP announced it has entered into a Memorandum of Understanding (MOU) with Sidra Medicine, a specialty healthcare organization for women, children and young people in Qatar.
Experts in the Hemostasis and Thrombosis Center at CHOP Provide Expert Commentary on Hemophilia
Leslie Raffini, MD, and Regina Butler, RN, were quoted in the Philadelphia Inquirer on a story featuring a CHOP patient family living with hemophilia, an inherited bleeding disorder that prevents blood from clotting properly.
NIH Awards Penn Medicine and Children’s Hospital of Philadelphia $26 Million Grant to Develop Therapies for Rare Newborn Genetic Diseases
A Penn Medicine and CHOP team will seek to develop treatments for three rare, incurable genetic diseases with the help of a $26 million grant from the National Institutes of Health.
CHOP Expert Breaks Down Latest Hemophilia A Gene Therapy Data
CHOP gene therapy expert Dr. Lindsey George reacts to a phase 3 hemophilia gene therapy study in an editorial in the New England Journal of Medicine.
CHOP Will Be Provider in Independence Blue Cross’s Gene Therapy Network
CHOP will be a provider in Independence Blue Cross’s new Advanced Network for Gene-Based Therapeutics, effective March 1, 2023.
First Approved CAR T-Cell Therapy Shows Continued Benefits Five Years Later
New data on show CAR T-cell therapy leads to durable remission and long-term survival in children and young adults with relapsed or refractory B-ALL.
Two New Treatments for Spinal Muscular Atrophy Offer Hope
Two new treatments are giving children with spinal muscular atrophy hope. CHOP is on the forefront of delivering care that is changing children’s lives.
‘I Can See It!’ — From Idea to Astonishing Result
Find out how a bold idea led to an astonishing cure for a certain childhood blindness, and learn about the future of gene therapy to treat children, like Hannah.
CHOP Hematologist Dr. Lindsey George Receives 2019 Clinical Achievement Research Award
Dr. George was recognized for the first gene therapy clinical trial to report a cure of hemophilia B patients.