Experimental Gene Therapy for Beta Thalassemia: Aliya’s Story
For the first 30 years of her life, Aliya needed monthly blood transfusions for her inherited blood disorder. A gene therapy changed everything.
Thalassemia Center Patient Stories
Every person on your child's team has the same goal: to see your child thrive. We provide medical care, emotional counseling and much more. We make sure your entire family gets the support you need.
Appointments and referrals
Beta Thalassemia Major: Mia’s Story
From the time she was just a few months old, Mia needed blood transfusions due to her rare blood disease. A bone marrow transplant changed everything.
Beta Thalassemia Major: Nicholas's Story
Beta thalassemia major forced Nicholas to undergo regular blood transfusions until he received a lifesaving bone marrow transplant.