Cure Spinal Muscular Atrophy funds and directs the leading spinal muscular atrophy research programs to develop a treatment and cure for the disease.

PPMD provides information about Duchenne muscular dystrophy, the most common fatal genetic disorder diagnosed in childhood, affecting approximately 1 in every 3,500 live male births.

The mission of the SMA Foundation is to accelerate the development of a treatment for spinal muscular atrophy, the number one genetic killer of infants and toddlers.