Skip to main content

Side Menu Card

Research Studies

Mitochondrial Medicine Program Research Studies

Find research studies available to children cared for by the Mitochondrial Medicine Program team.

Appointments and referrals

Recruitment Status

Study categories

Eligible age

DCA Trial in PDC Deficiency

We are studying an investigational drug called sodium dichloroacetate (DCA). Investigational means that the study drug has not been approved by the US Food and Drug Administration (FDA) and that its use in this study is experimental. This a purpose of this research study is to determine whether DCA is a helpful treatment for patient with pyruvate dehydrogenase complex (PDC) deficiency (PDCD).

Phase: Phase III

Actively recruiting: No

Category: Children

Jump back to top