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DCA Trial in PDC Deficiency

DCA Trial in PDC Deficiency

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If you are interested in participating in the study or want to learn more, please get in touch. Contact us
This study is no longer recruiting.

Description

We are studying an investigational drug called sodium dichloroacetate (DCA). Investigational means that the study drug has not been approved by the US Food and Drug Administration (FDA) and that its use in this study is experimental. This a purpose of this research study is to determine whether DCA is a helpful treatment for patient with pyruvate dehydrogenase complex (PDC) deficiency (PDCD).

Eligibility and criteria


IRB Number:
17-014294
Eligible age range:
6 months - 17 years
Clinical trial phase:
Phase III
Official title:
Trial of DCA in PDC Deficiency

What to expect


Smiling CHOP patient holding shopping bag

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