DCA Trial in PDC Deficiency
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Description
We are studying an investigational drug called sodium dichloroacetate (DCA). Investigational means that the study drug has not been approved by the US Food and Drug Administration (FDA) and that its use in this study is experimental. This a purpose of this research study is to determine whether DCA is a helpful treatment for patient with pyruvate dehydrogenase complex (PDC) deficiency (PDCD).
Eligibility and criteria
IRB Number:
17-014294
Eligible age range:
Clinical trial phase:
Phase III
Official title:
What to expect
Related specialties
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