An FDA-approved gene therapy eliminates acute pain episodes for people with sickle cell disease and transforms their life expectancy.

For years, sickle cell disease caused frequent pain crises and hospitalizations for Asher. A curative therapy has eliminated those harrowing experiences.

Sickle cell disease brings constant fear of life-threatening complications. A successful bone marrow transplant ended those fears for Dallas and her family.

From the time she was just a few months old, Mia needed blood transfusions due to her rare blood disease. A bone marrow transplant changed everything.

Beta thalassemia major forced Nicholas to undergo regular blood transfusions until he received a lifesaving bone marrow transplant.

Now 12, Caylin’s regular visits to CHOP for sickle cell disease treatment have inspired her love for comparing numbers, gathering data and experimenting.

Diagnosed with sickle cell disease as a baby, Nadir continues to receive comprehensive care from CHOP's Comprehensive Sickle Cell Center. 

Diagnosed with sickle cell disease before she was even born, Naomi is thriving today thanks to the care and support from her team at CHOP's Comprehensive Sickle Cell Center.