Children's Hospital of Philadelphia (CHOP) is a leader in developing gene therapy for hemophilia. We have made research breakthroughs in the molecular basis of blood clotting, and we have extensive experience in caring for patients. For these reasons, the NoT Bleeding Program can give your family the answers you need when it comes to caring for your child with a bleeding disorder.

World-renowned team

The NoT Bleeding Program is co-led by a team of world-class experts who together have more than two decades of clinical experience in gene therapy for hemophilia and in advanced care for patients with bleeding disorders.

• Lindsey George, MD, is a physician-scientist internationally known for her leadership in hemophilia A and B gene therapy clinical trials. She has served as an invited expert for the U.S. Food and Drug Administration on hemophilia gene therapy.
• Rodney Camire, PhD, is an international expert on the biology of blood coagulation.
• Benjamin Samelson-Jones, MD, PhD, has been a clinical investigator for gene therapy clinical trials for more than eight years.
• Leslie Raffini, MD, MSCE, is the Medical Director of CHOP’s Hemostasis and Thrombosis Center.
• Bhavya Doshi, MD, is a physician-scientist with expertise in hemostasis and immunology. She is also an Assistant Director of CHOP’s Clinical Coagulation Laboratory.

Care beyond medical needs

At our program, your child and family will have a team that supports you in every way. Among them:

• Dedicated nurses help you with scheduling appointments, understanding insurance and referrals, and coordinating your child’s care.
• Social workers help your child and family cope with the emotional and practical challenges of an ongoing illness.
• Genetic counselors can help you understand the genetic causes of bleeding disorders.
• Financial counselors help your family manage any financial concerns related to your child’s care, including the cost of gene therapy.

We are here to answer any questions you might have about your child’s bleeding disorder and their treatment options.