About Hemophilia
Hemophilia is a genetic disease that prevents blood from clotting properly leading to prolonged internal and external bleeding. Read more hemophilia and the existing treatments.
Resources
Novel Therapeutics for Bleeding Disorders (NoT Bleeding) Program Resources
Our Novel Therapeutics for Bleeding Disorders (NoT Bleeding) Program experts have created this list of resources to help you keep your child safe and well.
Contact us
Search Resources
Frequently Asked Questions about Gene Therapy for Hemophilia
Explore answers to the most common questions asked about gene therapy for hemophilia.
Gene Therapy in Hemophilia
View interactive webinars, educational resources and the latest news about hemophilia.