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Research Studies

Division of Hematology Research Studies

Find research studies available to children cared for by the Division of Hematology team.

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Eligible age

ENERGY Study

The ENERGY study is for adults (ages 18 and up) with warm Autoimmune Hemolytic Anemia (wAIHA) who are currently receiving treatment or have previously received treatment. The goal of the study is to see if the study drug, Nipocalimab is safe and effective in the treatment of wAIHA. Nipocalimab is an investigational medication designed to stop your immune system from destroying your red blood cells.

You may be able to join the study if you are:

  • 18 years of age or older
  • Diagnosed with wAIHA for at least 3 months
  • Currently receiving treatment or have previously received treatment for wAIHA
  • Have platelet counts of more than 30,000/ L and Hemoglobin less than 10 g/dL

Other study requirements will apply.

Phase: Phase II, Phase III

Actively recruiting: No

Category: Adults

HGB-212: Phase 3 Beta Thalassemia LentiGlobin BB305 Gene Therapy Trial

Individuals with a certain type of beta thalassemia that is treated with regular transfusions, and who are 50 years old and younger, may be able to participate. A number of screening tests will be done to determine if subjects can participate. These include review of your past medical history, blood and urine tests, bone marrow aspirate/biopsy, bone age/ DEXA scan, heart ultrasound, electrocardiogram, magnetic resonance imaging (MRI) of the heart and liver, and liver biopsy. If eligible, blood stem cells will be collected by apheresis or by bone marrow harvest. These stem cells will then have a healthy beta globin gene inserted. You will then be hospitalized and chemotherapy will be given to empty out the bone marrow. The stem cells, with the inserted gene, will then be given back to you. You will be followed for side effects and to see if the inserted gene helps you make hemoglobin.

Phase: Phase III

Actively recruiting: No

Category: Adults, Children, MRI/Imaging Studies

Conditions: Beta Thalassemia (Cooley's Anemia)

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